Patient-reported outcome measures in inherited retinal degeneration gene therapy trials
نویسندگان
چکیده
منابع مشابه
Gene therapy for inherited retinal degeneration.
Research into the molecular and genetic basis of disease is continually expanding and improving the prospects for rational treatments. Of these, gene therapy (here defined as the introduction of genetic material into human cells) may ultimately oVer the greatest scope. This article provides a perspective on the potential for gene therapy for treating inherited retinal degenerations, along with ...
متن کاملInherited Retinal Degeneration: Genetics, Disease Characterization, and Outcome Measures
Department of Ophthalmology & Visual Science, University of Michigan, Ann Arbor, MI 48105, USA Department of Ophthalmology, Fondazione Policlinico Universitario A. Gemelli, Università Cattolica del S. Cuore, Rome, Italy Department of Ophthalmology, Mie University Graduate School of Medicine, Tsu, Japan Moorfields Eye Hospital, 162 City Road, London EC1V 2PD, UK Institute of Ophthalmology, Unive...
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Yoga therapists are interested in knowing whether their therapeutic interventions are helpful in improving health and wellbeing in their yoga therapy clients. However, few yoga therapists use standardized, reliable, and valid questionnaires to determine the therapeutic effectiveness of their treatments. Patient-reported outcome (PRO) measures are paper or web-based questionnaires used to assess...
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1Dartmouth Institute for Health Policy and Clinical Practice, Geisel School of Medicine, Dartmouth College, 35 Centerra Parkway, Suite 300, Lebanon, NH 03766, USA; 2Dartmouth-Hitchcock Health, Lebanon, NH, USA ; 3 Department of Learning, Informatics, Management and Ethics, Karolinska Institutet, Sweden ; 4Rare Diseases Sweden, Stockholm, Sweden ; 5Genia, Stockholm, Sweden ; 6Hansen Law, Stockho...
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In recent years, there has been an increased focus on placing patients at the center of health care research and evaluating clinical care in order to improve their experience and ensure that research is both robust and of maximum value for the use of medicinal products, therapy, or health services. This paper provides an overview of patients' involvement in clinical research and service evaluat...
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ژورنال
عنوان ژورنال: Ophthalmic Genetics
سال: 2020
ISSN: 1381-6810,1744-5094
DOI: 10.1080/13816810.2020.1731836